To deliver genes directly to motor neurons from a minimally invasive, peripheral injection site.
About
Amyotrophic Lateral Sclerosis (ALS) is a progressive neurodegenerative disease affecting motor neurons that leads to progressive paralysis and premature death. There is a major unmet need for effective therapeutics. While gene therapy has promise, existing delivery technologies have limitations. Prof Nicholas Mazarakis has developed novel, targeted vectors designed to deliver genes directly to motor neurons from a minimally invasive, peripheral injection site. We have has filed patents for these lentiviral vectors and is seeking co-development or licensing partners for this technology. Please press “Connect” and we will send you 6 supporting Powerpoint slides on this technology. When contacting us, please quote reference code 6646.